Disease Thesaurus

While there are generally accepted names for most genetically inherited disease and non-inheritable genetic conditions, several go by a variety of names. This Disease Thesaurus offers a simple way to display a disease name and any naming convention associated with it.
Gene | Disease Name | Alternative Name 1 | Alternative Name 2 | Alternative Name 3 | Alternative Name 4 | Alternative Name 5 | Alternative Name 6 | Alternative Name 7 | Alternative Name 8 | Alternative Name 9 | Alternative Name 10 | Alternative Name 11 | Alternative Name 12 | Alternative Name 13 | Alternative Name 14 | Alternative Name 15 |
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ABCC8 | ABCC8-Related Hyperinsulinism | Congenital Hyperinsulinism | Familial Hyperinsulinism | Hyperinsulinemia Hypoglycemia Of Infancy | Infancy Hyperinsulinemia Hypoglycemia | Neonatal Hyperinsulinism | Persistent Hyperinsulinemia Hypoglycemia Of Infancy | Persistent Hyperinsulinemic Hypoglycemia | PHHI Hypoglycemia | |||||||
ACADM | Medium Chain Acyl-CoA Dehydrogenase Deficiency | Carnitine Deficiency Secondary To Medium-Chain Acyl-CoA Dehydrogenase Deficiency | MCADH Deficiency | MCAD Deficiency | Deficiency Of Medium-Chain Acyl-CoA Dehydrogenase | ACADM Deficiency | MCADD | |||||||||
ACADS | Short Chain Acyl-CoA Dehydrogenase Deficiency | Short Chain Acyl-CoA Dehydrogenase Deficiency | Short Chain Acyl-Coenzyme A Dehydrogenase Deficiency | Lipid-Storage Myopathy Secondary To Short-Chain Acyl-CoA Dehydrogenase Deficiency | Deficiency Of Short-Chain Acyl-CoA Dehydrogenase | ACADS Deficiency | SCADH Deficiency | SCADD | SCAD Deficiency | |||||||
ACADVL | Very Long Chain Acyl-CoA Dehydrogenase Deficiency | Acyl-CoA Dehydrogenase Very Long Chain Deficiency | Very Long-Chain Acyl Coenzyme A Dehydrogenase Deficiency | Galactose-1-Phosphate Uridyl-Transferase Deficiency Disease | VLCAD-H | ACADVL | ||||||||||
ADAMTS2 | Ehlers-Danlos Type Viic | Ehlers-Danlos Syndrome Dermatosparaxis Type | Dermatosparaxis | EDS VIIC | EDS7C | |||||||||||
AGA | Aspartylglycosaminuria | AGA Deficiency | Aspartylglucosaminidase Deficiency | Glycoasparaginase | AGU | Glycosylasparaginase Deficiency | ||||||||||
AGL | Glycogen Storage Disease Type Iii | GSD III | GDE Deficiency | Amylo-1 6-Glucosidase Deficiency | Limit Dextrinosis | Cori Disease | Forbes Disease | Glycogen Debrancher Deficiency | AGL Deficiency | |||||||
AGXT | Primary Hyperoxaluria Type 1 | Serine:Pyruvate Aminotransferase Deficiency | Alanine-Glyoxylate Aminotransferase Deficiency | Hepatic Agt Deficiency | HP1 | PH1 | Peroxisomal Alanine:Glyoxylate Aminotransferase Deficiency | Oxalosis I | Glycolic Aciduria | Hyperoxaluria Primary Type 1 | ||||||
AIRE | Polyglandular Autoimmune Syndrome Type 1 | AIRE Deficiency | APECED | APS1 | APS Type 1 | Autoimmune Polyendocrinopathy-Candidiasis-Ectodermal Dystrophy | Autoimmune Polyendocrinopathy Syndrome Type 1 | Autoimmune Polyendocrinopathy With Candidiasis And Ectodermal Dystrophy | Autoimmune Syndrome Type I Polyglandular | PGA I | Polyendocrinopathy-Candidiasis-Ectodermal-Dystrophy Autoimmune | Polyglandular Type I Autoimmune Syndrome | ||||
ALDH3A2 | Sjogren-Larsson Syndrome | Congenital Icthyosis Mental Retardation Spasticity Syndrome | FALDH Deficiency | Fatty Aldehyde Dehydrogenase Deficiency | Ichthyosis Oligophrenia Syndrome | |||||||||||
ALDOB | Hereditary Fructose Intolerance | ALDOB Deficiency | Aldolase B Deficiency | Fructose-1 6-Biphosphate Aldolase Deficiency | Fructose-1-Phosphate Aldolase Deficiency | Fructose Aldolase B Deficiency | Fructose Intolerance | Fructosemia | ||||||||
ALPL | Hypophosphatasia Autosomal Recessive | Deficiency Of Alkaline Phosphatase | Phosphoethanolaminuria | |||||||||||||
ARSA | Metachromatic Leukodystrophy | ARSA Deficiency | Arylsulfatase A Deficiency Disease | Cerebral Sclerosis Diffuse Metachromatic Form | Cerebroside Sulphatase Deficiency Disease | Greenfield Disease | Metachromatic Leukoencephalopathy | MLD | Sulfatide Lipidosis | Sulfatidosis | ||||||
ASPA | Canavan Disease | ACY2 Deficiency | Aminoacylase 2 Deficiency | Aspa Deficiency | Aspartoacylase Deficiency | Asp Deficiency | Canavan-Van Bogaert-Bertrand Disease | Leukodystrophy Spongiform | Spongy Degeneration Of Central Nervous System | Spongy Degeneration Of The Brain | Spongy Degeneration Of White Matter In Infancy | Van Bogaert-Bertrand Syndrome | Von Bogaert-Bertrand Disease | |||
ASS1 | Citrullinemia Type 1 | Cit | Citrullinuria | |||||||||||||
ATM | Ataxia-Telangiectasia | Louis-Bar Syndrome | AT | AT1 | ATM | Cerebello-Oculocutaneous Telangiectasia | ||||||||||
ATP7B | Wilson Disease | Hepatolenticular Degeneration Syndrome | WD | WND | Wilson Disease | Copper Storage Disease | Wilson’s Disease | |||||||||
BBS1 | Bardet-Biedl Syndrome Bbs1-Related | Bbs1-Related Bardet-Biedl Syndrome | BBS1 | Bardet-Biedl Syndrome 1 | Bardet-Biedl Syndrome | |||||||||||
BBS10 | Bardet-Biedl Syndrome Bbs10-Related | Bbs10-Related Bardet-Biedl Syndrome | Bardet-Biedl Syndrome | BBS10 | Bardet-Biedl Syndrome 10 | |||||||||||
BCHE | Pseudocholinesterase Deficiency | Butyrylcholinesterase Deficiency | Cholinesterase Ii Deficiency | Deficiency Of Butyrylcholine Esterase | Pseudocholinesterase E1 Deficiency | Succinylcholine Sensitivity | Suxamethonium Sensitivity | |||||||||
BCKDHA/BCKDHB | Maple Syrup Urine Disease Type 1 | BCKD Deficiency | Branched-Chain Alpha-Keto Acid Dehydrogenase Deficiency | Branched-Chain Ketoaciduria | Ketoacidemia | MSUD | ||||||||||
BCS1L | Gracile Syndrome | Fellman Syndrome | Finnish Lactic Acidosis With Hepatic Hemosiderosis | Finnish Lethal Neonatal Metabolic Syndrome | Growth Retardation Amino Aciduria Cholestasis Iron Overload Lactic Acidosis And Early Death | Finnish Lactic Acidosis With Hepatic Hemosiderosis | ||||||||||
BLM | Bloom Syndrome | BLS | BLM | Bloom’s Syndrome | BS | Bloom Syndrome | Bloom-Torre-Machacek Syndrome | |||||||||
BTD | Biotinidase Deficiency | Late-Onset Biotin-Responsive Multiple Carboxylase Deficiency | Btd Deficiency | Late-Onset Multiple Carboxylase Deficiency | Multiple Carboxylase Deficiency | |||||||||||
CBS | Homocystinuria Caused By Cystathionine Beta-Synthase Deficiency | Homocystinuria Caused By CBS Deficiency | Cystathionine Beta-Synthase Deficiency | CBS Deficiency | Cystathionine Beta-Synthase Deficiency Homocystinuria | Homocystinuria Caused By Cystathionine Beta-Synthase Deficiency | ||||||||||
CFTR | Cystic Fibrosis | Mucoviscidosis | CF | CFTR-Related Disorders | Fibrocystic Disease Of Pancreas | |||||||||||
CHM | Choroideremia | Progressive Tapetochoroidal Dystrophy | CHM | Choroideremia | TCD | Choroidal Sclerosis | ||||||||||
CLN3 | Cln3-Related Neuronal Ceroid Lipofuscinosis | Vogt-Spielmeyer Disease | Batten Disease | Neuronal Ceroid-Lipofuscinoses | Cln3-Related Neuronal Ceroid-Lipofuscinosis | Spielmeyer-Sjogren Disease | Neuronal Ceroid Lipofuscinosis 3 | |||||||||
CLN5 | Cln5-Related Neuronal Ceroid Lipofuscinosis | Neuronal Ceroid Lipofuscinosis 5 | Finnish Variant Neuronal Ceroid-Lipofuscinosis | Cln5-Related Neuronal Ceroid-Lipofuscinosis | Neuronal Ceroid-Lipofuscinoses | |||||||||||
CLN8 | Northern Epilepsy | CLN8-Related Neuronal Ceroid-Lipofuscinosis | Neuronal Ceroid Lipofuscinosis 8 | Neuronal Ceroid-Lipofuscinoses | ||||||||||||
CLRN1 | Usher Syndrome Type 3 | Deafness-Retinitis Pigmentosa Syndrome | Dystrophia Retinae Pigmentosa-Dysostosis Syndrome | Graefe-Usher Syndrome | Hallgren Syndrome | Retinitis Pigmentosa-Deafness Syndrome | Usher’s Syndrome | |||||||||
CNGB3 | Achromatopsia | Rod Monochromatism | Total Color Blindness | |||||||||||||
COL4A4 | Alport Syndrome Autosomal Recessive | Congenital Hereditary Hematuria | Hematuria-Nephropathy-Deafness Syndrome | Hematuric Hereditary Nephritis | Hemorrhagic Familial Nephritis | Hemorrhagic Hereditary Nephritis | Hereditary Familial Congenital Hemorrhagic Nephritis | Hereditary Hematuria Syndrome | Hereditary Interstitial Pyelonephritis | Hereditary Nephritis | ||||||
CPT1A | Carnitine Palmitoyltransferase Ia Deficiency | CPT1A Deficiency | Hepatic CPT Deficiency Type I | Carnitine Palmitoyltransferase I Deficiency | Hepatic CPT1 | CPT I Deficiency | Hepatic Carnitine Palmitoyltransferase 1 Deficiency | L-CPT 1 Deficiency | Carnitine Palmitoyltransferase IA Deficiency | |||||||
CPT2 | Carnitine Palmitoyltransferase Ii Deficiency | Carnitine Palmitoyltransferase 2 Deficiency | CPT2 Deficiency | |||||||||||||
CTNS | Cystinosis | Cystine Storage Disease | ||||||||||||||
CTSK | Pycnodysostosis | PYCD | PKND | Pyknodysostosis | ||||||||||||
DHCR7 | Smith-Lemli-Opitz Syndrome | 7-Dehydrocholesterol Reductase Deficiency | RSH Syndrome | SLOS | Slo Syndrome | Rutledge Lethal Multiple Congenital Anomaly Syndrome | ||||||||||
DHDDS | Retinitis Pigmentosa 59 | Cone-Rod Retinal Dystrophy | Pigmentary Retinopathy | Rod-Cone Dystrophy | RP | Tapetoretinal Degeneration | ||||||||||
DLD | Dihydrolipoamide Dehydrogenase Deficiency | Msud3 | Lipoamide Dehydrogenase Deficiency | Maple Syrup Urine Disease Type Iii | Lipoamide Dehydrogenase Deficiency | Maple Syrup Urine Disease Type 3 | MSUD Type 3 | E-3 Deficient MSUD | ||||||||
DPYD | Hereditary Thymine-Uraciluria | Dihydropyrimidine Dehydrogenase Deficiency | Dihydropyrimidinuria | DPD Deficiency | Familial Pyrimidemia | |||||||||||
F11 | Factor Xi Deficiency | Rosenthal Syndrome | PTA Deficiency | F11 Deficiency | Plasma Thromboplastin Antecedent Deficiency | Factor 11 Deficiency | Hemophilia C | |||||||||
F2 | Prothrombin Thrombophilia | Hyperprothrombinemia | Prothrombin G20210a Thrombophilia | Venous Thromboembolism | Factor Ii Deficiency | Dysprothrombinemia | ||||||||||
F5 | Factor V Leiden Thrombophilia | APC Resistance Leiden Type | Hereditary Resistance To Activated Protein C | Factor V Leiden Mutation | Parahemophilia | Owren Parahemophilia | Labile Factor Deficiency | Factor V Deficiency | ||||||||
FAH | Tyrosinemia Type I | Hepatorenal Tyrosinemia | Fah Deficiency | Hereditary Tyrosinemia Type I | Fumarylacetoacetase Deficiency | Fumarylacetoacetate Hydrolase Deficiency | Hypertyrosinemia | |||||||||
FANCC | Fanconi Anemia Type C | Fanconi Anemia | Fanconi Pancytopenia Type 3 | Fancc-Related Fanconi Anemia | FANCC | Complementation Group C Fanconi Anemia | Fanconi Hypoplastic Anemia | Fanconi Pancytopenia | FA | Fanconi Panmyelopathy | ||||||
FMR1 | Fragile X | FRAXA Syndrome | Fra(X) Syndrome | FXS | Marker X Syndrome | Martin-Bell Syndrome | X-Linked Mental Retardation And Macroorchidism | |||||||||
FKTN | Walker-Warburg | Cerebroocular Dysplasia-Muscular Dystrophy Syndrome | Warburg Syndrome | Chemke Syndrome | Cod-Md Syndrome | HARD Syndrome | Hydrocephalus Agyria And Retinal Dysplasia | Walker-Warburg Congenital Muscular Dystrophy | Pagon Syndrome | |||||||
G6PC | Glycogen Storage Disease Type Ia | Glycogen Storage Disease I | Von Gierke’s Disease | Hepatorenal Form Of Glycogen Storage Disease | Hepatorenal Glycogenosis | GSD1A | Glucose-6-Phosphatase Deficiency | Von Gierke Disease | ||||||||
G6PD | Glucose-6-Phosphate Dehydrogenase Deficiency | G6PDD | G6PD Deficiency | |||||||||||||
GAA | Pompe Disease | Acid Maltase Deficiency | Alpha-1 4-Glucosidase Deficiency | AMD | Alpha-Glucosidase Deficiency | Glycogenosis Type II | Glycogen Storage Disease Type II | GSD II | ||||||||
GALC | Krabbe Disease | Diffuse Globoid Body Sclerosis | Galactosylceramidase Deficiency Disease | Galactosylceramide Lipidosis | Galactosylcerebrosidase Deficiency | Galactosylsphingosine Lipidosis | Galc Deficiency | GCL | GLD | Psychosine Lipidosis | ||||||
GALT | Galactosemia | Classic Galactosemia | Epimerase Deficiency Galactosemia | Galactokinase Deficiency Disease | Galactose-1-Phosphate Uridyl-Transferase Deficiency Disease | Galactose Epimerase Deficiency | Galt Deficiency | Udp-Galactose-4-Epimerase Deficiency Disease | Udpglucose 4-Epimerase Deficiency Disease | Udpglucose Hexose-1-Phosphate Uridylyltransferase Deficiency | Utp Hexose-1-Phosphate Uridylyltransferase Deficiency | |||||
GBA | Gaucher Disease | Cerebroside Lipidosis Syndrome | Gaucher’s Disease | Gaucher Splenomegaly | Gaucher Syndrome | GD | Glucocerebrosidase Deficiency | Glucocerebrosidosis | Glucosylceramidase Deficiency | Glucosylceramide Beta-Glucosidase Deficiency | Glucosylceramide Lipidosis | Glucosyl Cerebroside Lipidosis | Kerasin Histiocytosis | Kerasin Lipoidosis | Kerasin Thesaurismosis | Lipoid Histiocytosis (Kerasin Type) |
GCDH | Glutaric Acidemia Type 1 | GA I | Glutaric Acidemia I | Glutaric Aciduria I | Glutaryl-Coa Dehydrogenase Deficiency | |||||||||||
GJB2 | Gjb2-Related Dfnb1 Nonsyndromic Hearing Loss And Deafness | Dfnb1 Nonsyndromic Hearing Loss And Deafness | DDNB1 | Autosomal Recessive Deafness 1 | Neurosensory Nonsyndromic Recessive Deafness 1 | Isolated Deafness | Undifferentiated Deafness | Nonsyndromic Hearing Impairment | Nonsyndromic Hearing Loss | |||||||
GNE | Inclusion Body Myopathy 2 | Distal Myopathy With Rimmed Vacuoles | DMRV | Hereditary Inclusion Body Myopathy | HIBM | IBM2 | Autosomal Recessive Inclusion Body Myopathy | Quadriceps-Sparing Inclusion Body Myopathy | QSM | Nonaka Myopathy | Rimmed Vacuole Myopathy | |||||
GRHPR | Primary Hyperoxaluria Type 2 | D-Glycerate Dehydrogenase Deficiency | Glyceric Aciduria | Glycolic Aciduria | Oxalosis | Primary Oxaluria | HP2 | |||||||||
HADHA | Long Chain 3-Hydroxyacyl-Coa Dehydrogenase Deficiency | LCHAD Deficiency | Trifunctional Protein Deficiency Type 1 | Long-Chain 3-Hydroxyacyl-Coenzyme A Dehydrogenase Deficiency | Long-Chain 3-Oh Acyl-Coa Dehydrogenase Deficiency | |||||||||||
HBA1/HBA2 | Alpha Thalassemia | [None Found] | ||||||||||||||
HBB | Beta Thalassemia | Erythroblastic Anemia | Mediterranean Anemia | Microcytemia Beta Type | ||||||||||||
HBB | Sickle Cell | Sickle Cell Disease | Sickle Cell Anemia | Hbs Disease | Hemoglobin S Disease | SCD | Sickle Cell Disorder | Sickling Disorder Due To Hemoglobin S | ||||||||
HEXA | Tay-Sachs Disease | Hexosaminidase A Deficiency | HEX A Deficiency | Gm2 Gangliosidosis | ||||||||||||
HFE | Hfe-Associated Hereditary Hemochromatosis | Bronzed Cirrhosis | Bronze Diabetes | Familial Hemochromatosis | Genetic Hemochromatosis | Haemochromatosis | HC | Hemochromatoses | Hlah | Hh | Iron Storage Disorder | Pigmentary Cirrhosis | Primary Hemochromatosis | Troisier-Hanot-Chauffard Syndrome | Von Recklenhausen-Applebaum Disease | |
HGD | Alkaptonuria | AKU | Alcaptonuria | Homogentisic Acid Oxidase Deficiency | Homogentisic Acidura | |||||||||||
HSD17B4 | D-Bifunctional Protein Deficiency | 17-Beta-Hydroxysteroid Dehydrogenase Iv Deficiency | Bifunctional Peroxisomal Enzyme Deficiency | DBP Deficiency | Pbfe Deficiency | Peroxisomal Bifunctional Enzyme Deficiency | Pseudo-Zellweger Syndrome | Zellweger-Like Syndrome | ||||||||
IDUA | Hurler Syndrome | Alpha-L-Iduronidase Deficiency | Mucopolysaccharidosis Type Ih | MPS I | Idua Deficiency | Mucopolysaccharidosis Type I | Hurler’s Disease | Gargoylism | ||||||||
IKBKAP | Familial Dysautonomia | FD | HSAN3 | HSAN III | Riley-Day Syndrome | Hereditary Sensory And Autonomic Neuropathy Type 3 | ||||||||||
IVD | Isovaleric Acidemia | Isovaleric Acid-Coa Dehydrogenase Deficiency | Isovaleryl-Coa Dehydrogenase Deficiency | IVA | IVD Deficiency | |||||||||||
LAMA3 | Lama3-Related Junctional Epidermolysis Bullosa | JEB | ||||||||||||||
LAMB3 | Lamb3-Related Junctional Epidermolysis Bullosa | JEB | ||||||||||||||
LAMC2 | Lamc2-Related Junctional Epidermolysis Bullosa | JEB | ||||||||||||||
MAN2B1 | Alpha-Mannosidosis | Alpha-D-Mannosidosis | Alpha-Mannosidase B Deficiency | Alpha-Mannosidase Deficiency | Lysosomal Alpha B Mannosidosis | Lysosomal Alpha-D-Mannosidase Deficiency | Mannosidosis | |||||||||
MCOLN1 | Mucolipidosis Iv | Ganglioside Sialidase Deficiency | ML4 | MLIV | Sialolipidosis | |||||||||||
MEFV | Familial Mediterranean Fever | Benign Paroxysmal Peritonitis | Familial Paroxysmal Polyserositis | FMF | MEF | Recurrent Polyserositis | Reimann Periodic Disease | Siegal-Cattan-Mamou Disease | Wolff Periodic Disease | |||||||
MLC1 | Megalencephalic Leukoencephalopathy With Subcortical Cysts | Infantile Leukoencephalopathy And Megalencephaly | Leukoencephalopathy With Swelling And A Discrepantly Mild Course | Leukoencephalopathy With Swelling And Cysts | LVM | MLC | Vacuolating Leukoencephalopathy | Vacuolating Megalencephalic Leukoencephalopathy With Subcortical Cysts | Van Der Knapp Disease | Vl | ||||||
MPI | Congenital Disorder Of Glycosylation Type Ib | SLSJ Syndrome | Saguenay-Lac Saint-Jean Syndrome | Gastrointestinal Type CDG | MPI Deficiency | CDG1B | Protein-Losing Enteropathy-Hepatic Fibrosis Syndrome | Mannosephosphate Isomerase Deficiency | ||||||||
MPL | Congenital Amegakaryocytic Thrombocytopenia | CAMT | ||||||||||||||
MTTP | Abetalipoproteinemia | Abetalipoproteinemia Neuropathy | Acanthocytosis | Apolipoprotein B Deficiency | Bassen-Kornzweig Syndrome | Betalipoprotein Deficiency Disease | Congenital Betalipoprotein Deficiency Syndrome | Microsomal Triglyceride Transfer Protein Deficiency Disease | ||||||||
NBN | Nijmegen Breakage Syndrome | Ataxia-Telangiectasia Variant 1 | Berlin Breakage Syndrome | Seemanova Syndrome | Microcephaly Normal Intelligence And Immunodeficiency | |||||||||||
NEB | Neb-Related Nemaline Myopathy | Nemaline Body Disease | Nemaline Rod Disease | Rod Body Disease | Rod-Body Myopathy | Rod Myopathy | ||||||||||
NOLA3 | Dyskeratosis Congenita Autosomal Recessive | Zinsser-Cole-Engman Syndrome | ||||||||||||||
NPC1 | Niemann-Pick Disease Type C | Lipid Histiocytosis | Neuronal Cholesterol Lipidosis | Neuronal Lipidosis | NPD | Sphingomyelinase Deficiency | Sphingomyelin/Cholesterol Lipidosis | Sphingomyelin Lipidosis | ||||||||
NPHS1 | Congenital Finnish Nephrosis | Nephrotic Syndrome Type 1 | Congenital Nephrosis | Finnish Congenital Nephrosis | ||||||||||||
NPHS2 | Steroid-Resistant Nephrotic Syndrome | [None Found] | ||||||||||||||
OPA3 | Costeff Optic Atrophy Syndrome | Costeff Syndrome | 3-Methylglutaconic Aciduria Type 3 | Autosomal Recessive Opa3 | Autosomal Recessive Optic Atrophy 3 | Nfantile Optic Atrophy With Chorea And Spastic Paraplegia | Iraqi Jewish Optic Atrophy Plus | MGA3 | MGA Type III | OPA3 Defect | Optic Atrophy Plus Syndrome | |||||
PAH | Phenylalanine Hydroxylase Deficiency | Folling Disease | Folling’s Disease | Phenylkaptonuria | PKU | Pah Deficiency | PKU | |||||||||
PCDH15 | Usher Syndrome Type 1f | USH1F | Deafness-Retinitis Pigmentosa Syndrome | Dystrophia Retinae Pigmentosa-Dysostosis Syndrome | Graefe-Usher Syndrome | Hallgren Syndrome | Retinitis Pigmentosa-Deafness Syndrome | Usher’s Syndrome | ||||||||
PEX1 | Pex1-Related Zellweger Syndrome Spectrum | Cerebrohepatorenal Syndrome | Peroxisome Biogenesis Disorders Zellweger Syndrome Spectrum | Zellweger Spectrum | ||||||||||||
PEX7 | Rhizomelic Chondrodysplasia Punctata Type 1 | RCP | RCDP | |||||||||||||
PHGDH | 3-Phosphoglycerate Dehydrogenase Deficiency | Phosphoglycerate Dehydrogenase Deficiency | 3-PGDH Deficiency | PHGDH Deficiency | ||||||||||||
PKHD1 | Autosomal Recessive Polycystic Kidney Disease | Polycystic Kidney Disease | PKD | Polycystic Renal Disease | ||||||||||||
PMM2 | Congenital Disorder Of Glycosylation Type Ia | Carbohydrate-Deficient Glycoprotein Syndrome Type 1a | Phosphomannomutase 2 Deficiency | CDG-IA | ||||||||||||
POMGNT1 | Muscle-Eye-Brain Disease | MEB | Congenital Muscular Dystrophy | |||||||||||||
PPT1 | Ppt1-Related Neuronal Ceroid Lipofuscinosis | Late-Infantile Neuronal Ceroid Lipofuscinosis | Jansky-Bielschowsky Disease | Late-Infantile Batten Disease | LINCL | |||||||||||
PROP1 | Prop1-Related Combined Pituitary Hormone Deficiency | CPHD | Panhypopituitarism | |||||||||||||
PYGM | Glycogen Storage Disease Type V | GSDV | Mcardle Disease | Glycogenosis 5 | Gsd Type V | Gsd 5 | Mcardle’s Disease | Mcardle Syndrome | Mcardle Type Glycogen Storage Disease | Muscle Glycogen Phosphorylase Deficiency | Muscle Phosphorylase Deficiency | Myophosphorylase Deficiency | Pygm Deficiency | |||
RMRP | Cartilage-Hair Hypoplasia | Cartilage-Hair Syndrome | CHH | Mckusick’s Metaphyseal Chondrodysplasia Syndrome | Recessive Metaphyseal Chondroplasia | |||||||||||
RS1 | X-Linked Juvenile Retinoschisis | Congenital X-Linked Retinoschisis | Juvenile Retinoschisis | Degenerative Retinoschisis | X-Linked Retinoschisis | |||||||||||
SACS | Arsacs | Spastic Ataxia Of Charlevoix-Saguenay | Charlevoix-Saguenay Spastic Ataxia | Autosomal Recessive Spastic Ataxia Of Charlevoix-Saguenay | Sacs | |||||||||||
SERPINA1 | Alpha-1 Antitrypsin Deficiency | AAT | AATD | Alpha-1 Protease Inhibitor Deficiency | Alpha-1 Related Emphysema | Genetic Emphysema | Hereditary Pulmonary Emphysema | Inherited Emphysema | ||||||||
SGCA | Limb-Girdle Muscular Dystrophy Type 2d | LGMD | Limb-Girdle Syndrome | Myopathic Limb-Girdle Syndrome | ||||||||||||
SGCB | Limb-Girdle Muscular Dystrophy Type 2e | LGMD | Limb-Girdle Syndrome | Myopathic Limb-Girdle Syndrome | ||||||||||||
SLC12A6 | Andermann Syndrome | ACCPN | Agenesis Of Corpus Callosum With Neuronopathy | Agenesis Of Corpus Callosum With Peripheral Neuropathy | Agenesis Of Corpus Callosum With Polyneuropathy | Charlevoix Disease | Hereditary Motor And Sensory Neuropathy With Agenesis Of The Corpus Callosum | HMSN/ACC | ||||||||
SLC17A5 | Salla Disease | Free Sialic Acid Storage Disease | N-Acetylneuraminic Acid Storage Disease | Nana Storage Disease | Sialuria Finnish Type | Sialic Acid Storage Disease | ||||||||||
SLC22A5 | Primary Carnitine Deficiency | Carnitine Transporter Deficiency | Carnitine Uptake Defect | Carnitine Uptake Deficiency | CUD | Renal Carnitine Transport Defect | Systemic Carnitine Deficiency | |||||||||
SLC26A2 | Sulfate Transporter-Related Osteochondrodysplasia | Recessive Multiple Epiphyseal Dysplasia | Achondrogenesis Type 1b | Diastrophic Dysplasia | Atelosteogenesis Type Ii | |||||||||||
SLC26A4 | Pendred Syndrome | Autosomal Recessive Sensorineural Hearing Impairment And Goiter | Deafness With Goiter | Goiter-Deafness Syndrome | ||||||||||||
SLC35A3 | Arthrogryposis Mental Retardation And Seizures (Amrs) | [None Found] | ||||||||||||||
SLC37A4 | Glycogen Storage Disease Type Ib | Glucose-6-Phosphate Deficiency | Glucose-6-Phosphate Transport Defect | GSD I | GSD Type I | Hepatorenal Form Of Glycogen Storage Disease | Hepatorenal Glycogenosis | Von Gierke Disease | ||||||||
SMN1 | Spinal Muscular Atrophy | Hereditary Motor Neuronopathy | Progressive Muscular Atrophy | Spinal Amyotrophy | Sma | |||||||||||
SMPD1 | Niemann-Pick Disease Smpd1-Associated | Lipid Histiocytosis | Neuronal Cholesterol Lipidosis | Neuronal Lipidosis | NPD | Sphingomyelinase Deficiency | Sphingomyelin/Cholesterol Lipidosis | Sphingomyelin Lipidosis | ||||||||
SUMF1 | Multiple Sulphatase Deficiency | Austin Syndrome | Juvenile Sulfatidosis Austin Type | MSD | Mucosulfatidosis | |||||||||||
TH | Segawa Syndrome | Autosomal Recessive Infantile Parkinsonism | Tyrosine Hydroxylase (Th) Deficiency | Th-Deficient Drd | ||||||||||||
TMEM216 | Joubert Syndrome 2 | JBTS2 | ||||||||||||||
TPP1 | Tpp1-Related Neuronal Ceroid Lipofuscinosis | Jansky-Bielschowsky Disease | Late-Infantile Batten Disease | LINCL | Neuronal Ceroid Lipofuscinosis Late-Infantile | |||||||||||
TTPA | Ataxia With Vitamin E Deficiency | Ataxia With Isolated Vitamin E Deficiency | AVED | Familial Isolated Vitamin E Deficiency | FIVE | Friedreich Ataxia Phenotype With Selective Vitamin E Deficiency | Friedreich-Like Ataxia | |||||||||
VPS13B | Cohen Syndrome | Norio Syndrome | Obesity-Hypotonia Syndrome | Pepper Syndrome | Prominent Incisors-Obesity-Hypotonia Syndrome | Hypotonia Obesity And Prominent Incisors |